Science7 min read
Diseases and Conditions Treated With Cord Blood Stem Cells
Cord blood stem cells are FDA-approved for treating dozens of serious conditions. Research is ongoing into many more. Here's a parent-friendly overview of what's established and what's still emerging.
Established uses (standard of care)
- Leukemias: acute lymphoblastic leukemia (ALL), acute myeloid leukemia (AML), chronic myeloid leukemia (CML)
- Lymphomas: Hodgkin and non-Hodgkin lymphoma
- Inherited blood disorders: sickle cell disease, thalassemia
- Bone marrow failure: aplastic anemia, Fanconi anemia
- Severe combined immunodeficiency (SCID) and other primary immunodeficiencies
- Certain metabolic disorders such as Hurler syndrome and Krabbe disease
Active research areas
- Cerebral palsy
- Autism spectrum disorders (early-stage trials)
- Type 1 diabetes
- Spinal cord injury
- Stroke recovery in adults